Original Research
Published on 24 Mar 2023
Early postnatal administration of an AAV9 gene therapy is safe and efficacious in CLN3 disease
in Genetics of Common and Rare Diseases
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- 18 citations
Original Research
Published on 24 Mar 2023
in Genetics of Common and Rare Diseases
Original Research
Published on 24 Mar 2023
in Genetics of Common and Rare Diseases
Editorial
Published on 24 Mar 2023
in Genetics of Common and Rare Diseases
Case Report
Published on 23 Mar 2023
in Genetics of Common and Rare Diseases
Original Research
Published on 23 Mar 2023
in Genetics of Common and Rare Diseases
Original Research
Published on 22 Mar 2023
in Genetics of Common and Rare Diseases
Case Report
Published on 22 Mar 2023
in Genetics of Common and Rare Diseases
Case Report
Published on 22 Mar 2023
in Genetics of Common and Rare Diseases
Case Report
Published on 21 Mar 2023
in Genetics of Common and Rare Diseases
Case Report
Published on 21 Mar 2023
in Genetics of Common and Rare Diseases
Original Research
Published on 21 Mar 2023
in Genetics of Common and Rare Diseases
Original Research
Published on 21 Mar 2023
in Genetics of Common and Rare Diseases
Case Report
Published on 21 Mar 2023
in Genetics of Common and Rare Diseases
Original Research
Published on 20 Mar 2023
in Genetics of Common and Rare Diseases
Original Research
Published on 20 Mar 2023
in Genetics of Common and Rare Diseases
Original Research
Published on 20 Mar 2023
in Genetics of Common and Rare Diseases
Original Research
Published on 17 Mar 2023
in Genetics of Common and Rare Diseases
Case Report
Published on 16 Mar 2023
in Genetics of Common and Rare Diseases
Original Research
Published on 16 Mar 2023
in Genetics of Common and Rare Diseases
Case Report
Published on 16 Mar 2023
in Genetics of Common and Rare Diseases
Mini Review
Published on 15 Mar 2023
in Genetics of Common and Rare Diseases
Original Research
Published on 14 Mar 2023
in Genetics of Common and Rare Diseases
Original Research
Published on 14 Mar 2023
in Genetics of Common and Rare Diseases
Case Report
Published on 10 Mar 2023
in Genetics of Common and Rare Diseases