Submission closed Genome Editing to Treat Cystic Fibrosis and Other Pulmonary Diseases Sriram VaidyanathanAmy L Ryan 22,594 views 5 articles
Submission closed Ex-Vivo and In-Vivo Genome Engineering for Metabolic and Neurometabolic Diseases Guilherme BaldoPasqualina ColellaNatalia Gomez-OspinaVasco Meneghini 29,229 views 5 articles
eBook Submission closed Therapeutic Gene Correction Strategies Based on CRISPR Systems or Other Engineered Site-specific Nucleases Ayal HendelRasmus O Bak 95,633 views 12 articles
eBook Submission closed Mutation-Specific Gene Editing for Blood Disorders Carsten Werner LedererPietro GenoveseAnnarita MiccioSjaak Philipsen 287,424 views 18 articles
Submission closed Genome Engineering and Gene Editing in Neuronal and Glial Cells Gabriele LignaniVania BroccoliJohan Jakobsson 83,494 views 6 articles